authors Li, Yanjie Polak, Urszula Bhalla, Angela D Rozwadowska, Natalia Butler, Jill Sergesketter David Lynch, MD, PhD Dent, Sharon Y R Napierala, Marek
has subject area Aconitate Hydratase Adenine Alleles Cell Differentiation Endodeoxyribonucleases Fibroblasts Friedreich Ataxia Genetic Therapy Guanine Heterozygote Humans Induced Pluripotent Stem Cells Introns K562 Cells Neurons Phenotype RNA, Messenger Trinucleotide Repeat Expansion Zinc Fingers