publication venue for
- Central Nervous System Therapeutic Targets in Friedreich Ataxia.. 31:1226-1236. 2020
- Successful gene therapy in older Rpe65-deficient dogs following subretinal injection of an adeno-associated vector expressing RPE65.. 24:883-93. 2013
- Long-term increase in mVEGF164 in mouse hindlimb muscle mediated by phage phiC31 integrase after nonviral DNA delivery.. 17:871-6. 2006
- Dystrophin gene repair in mdx muscle precursor cells in vitro and in vivo mediated by RNA-DNA chimeric oligonucleotides.. 13:707-18. 2002