Alglucosidase alfa enzyme replacement therapy as a therapeutic approach for glycogen storage disease type III. uri icon

authors

  • Sun, Baodong
  • Fredrickson, Keri
  • Austin, Stephanie
  • Tolun, Adviye A
  • Thurberg, Beth L
  • William E. Kraus, MD
  • Bali, Deeksha
  • Chen, Yuan-Tsong
  • Kishnani, Priya S

publication date

  • January 1, 2012